AAV.U7snRNA-Mediated Gene Therapy Vectors to Skip Exon 19 in Patients with DMDThis invention represents an improved, precision‑based AAV.U7snRNA‑mediated exon‑skipping gene‑therapy platform targeting exon 19 of the DMD gene to treat Duchenne and Becker muscular dystrophies. |
Tech ID2026-013 College(None) Licensing ManagerInventorsCategories(None) |
