Conventional Gene Therapy Approach for FOXG1

FOXG1 syndrome is a rare neurological and developmental disorder that usually affects children at infancy. Individuals with this disorder experience seizures, delayed development, intellectual disability, and mobility issues. Currently, there is no cure. Researchers at Nationwide Children’s Hospital designed a conventional gene therapy approach for FOXG1 by establishing vitro models and comparing data for FOXG1 cell lines and Rhett Syndrome cell lines. (need info. about the results of the 2021 pilot study)

Application:

Treatment for FOXG1

Stage of Application:

Pilot study undergoing.

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